A Study of Patients With Fabry Disease (US Specific)

Not yet recruitingOBSERVATIONAL
Enrollment

450

Participants

Timeline

Start Date

October 31, 2025

Primary Completion Date

June 30, 2032

Study Completion Date

June 30, 2032

Conditions
Fabry Disease
Interventions
DRUG

migalastat HCl

Non-interventional study of participants receiving migalastat HCl 150 mg

DRUG

ERT

Non-interventional study of participants receiving enzyme replacement therapy

Trial Locations (4)

22030

Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax

30322

Emory Genetics, Atlanta

63110

Washington University School of Medicine, St Louis

75204

Renal Disease Research Institute, Dallas

Sponsors
All Listed Sponsors
lead

Amicus Therapeutics

INDUSTRY

NCT06906367 - A Study of Patients With Fabry Disease (US Specific) | Biotech Hunter | Biotech Hunter