To Evaluate Long- Term Safety and Efficacy of Luspatercept

Active, not recruitingOBSERVATIONAL
Enrollment

350

Participants

Timeline

Start Date

April 30, 2023

Primary Completion Date

February 24, 2025

Study Completion Date

February 24, 2026

Conditions
Thalassemia Major
Interventions
DRUG

Luspatercept (ACE-536)

Luspatercept (ACE-536)

Trial Locations (1)

09121

UniversityCagliari, OspPed Microcitemico, Cagliari, Cagliari

All Listed Sponsors
lead

Fondazione per la Ricerca sulle Anemie ed Emoglobinopatie in Italia

OTHER