18
Participants
Start Date
May 14, 2025
Primary Completion Date
August 30, 2028
Study Completion Date
August 30, 2028
HM15421/GC1134A
SC
RECRUITING
University of Pittsburgh Medical Center Children's Hoispital of Pittsburgh, Pittsburgh
RECRUITING
Lysosomal and Rare Disorders Research and Treatment Center, Fairfax
RECRUITING
Pusan National University Children's Hospital in Yangsan, Yangsan
RECRUITING
University of Minnesota, Minneapolis
RECRUITING
David Geffen School of Medicine UCLA, UCLA Health, Los Angeles
RECRUITING
University of Kansas School of Medicine, Kansas City
RECRUITING
Children's Hospital Medical Center, Cincinnati
RECRUITING
Centro Medico IPAM, Rosario
RECRUITING
Hospital Italiano de Buenos Aires, Buenos Aires
RECRUITING
Yonsei University, College of Medicine, Seoul
Lead Sponsor
Collaborators (1)
Hanmi Pharmaceutical Company Limited
INDUSTRY
GC Biopharma Corp
INDUSTRY