NCT06844214 - A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 50 Years of Age With Non-congenital Myotonic Dystrophy Type 1 | Biotech Hunter

Enrollment

Participants

Timeline

Start Date

July 23, 2025

Primary Completion Date

February 28, 2029

Study Completion Date

February 28, 2030

Conditions

Myotonic Dystrophy

Interventions

BIOLOGICAL

SAR446268

Pharmaceutical form: Solution for infusion; Route of administration: IV infusion

Trial Locations (4)

RECRUITING

Columbia University Medical Center- Site Number : 8400003, New York

RECRUITING

University of Florida Health- Site Number : 8400005, Gainesville

RECRUITING

University of South Florida- Site Number : 8400001, Tampa

RECRUITING

Investigational Site Number : 0320001, Ciudad Autonoma Buenos Aires