NCT06817590 - Nucleoside Therapy in Patients With Telomere Biology Disorders | Biotech Hunter

Enrollment

Participants

Timeline

Start Date

September 30, 2025

Primary Completion Date

June 30, 2028

Study Completion Date

June 30, 2029

Conditions

Telomere Biology DisordersDyskeratosis CongenitaRevesz SyndromeHoyeraal Hreidarsson SyndromeTelomere Biology Disorders With Bone Marrow FailureInterstitial Lung Disease Due to Systemic Disease (Telomere Biology Disorder)Pulmonary Fibrosis, Familial (Telomere Biology Disorder)

Interventions

DRUG

deoxycytidine

Oral administration, in combination with deoxythymidine

DRUG

deoxythymidine

Oral administration, in combination with deoxycytidine

Trial Locations (1)

02115

RECRUITING

Boston Childrens Hospital, Boston

All Listed Sponsors

lead

Suneet Agarwal

OTHER