Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency

PHASE2RecruitingINTERVENTIONAL
Enrollment

15

Participants

Timeline

Start Date

January 1, 2025

Primary Completion Date

January 31, 2027

Study Completion Date

December 31, 2027

Conditions
Thymidine Kinase 2 (TK2 ) DeficiencyMitochondrial Myopathies
Interventions
DRUG

Doxecitine and Doxribtimine

A combination of doxecitine and doxribtimine is administered orally in 3 equal doses given approximately 6 to 8 hours apart .Dose will be increased if the tolerability profile is good.

Trial Locations (1)

28041

RECRUITING

Hospital Universitario 12 de Octubre, Madrid

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

UCB Pharma

INDUSTRY

lead

Cristina Domínguez González

OTHER

NCT06754098 - Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency | Biotech Hunter | Biotech Hunter