Safety and Efficacy Study of PUMCH-E101 Injection in Subjects with RDH12 Retinopathy

EARLY_PHASE1RecruitingINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

September 20, 2024

Primary Completion Date

December 31, 2027

Study Completion Date

January 4, 2030

Conditions
Inherited Retinal Diseases
Interventions
GENETIC

PUMCH-E101 Injection(Low dose)

Single intravitreal injection

GENETIC

PUMCH-E101 Injection(High dose)

Single intravitreal injection

Trial Locations (1)

100730

RECRUITING

Peking Union Medical College Hospital, Beijing

All Listed Sponsors
lead

Peking Union Medical College Hospital

OTHER