Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

RecruitingOBSERVATIONAL
Enrollment

200

Participants

Timeline

Start Date

June 6, 2025

Primary Completion Date

June 30, 2030

Study Completion Date

June 30, 2030

Conditions
Congenital Myotonic DystrophyChildhood Myotonic DystrophyMyotonic Dystrophy
Trial Locations (1)

23298

RECRUITING

Virginia Commonwealth University, Richmond

All Listed Sponsors
collaborator

National Institute of Neurological Disorders and Stroke (NINDS)

NIH

collaborator

SUNY Research Foundation

OTHER

collaborator

University of Minnesota

OTHER

collaborator

Roseman University of Health Sciences

OTHER

collaborator

University of California, San Diego

OTHER

collaborator

University of Glasgow

OTHER

collaborator

University of Kansas Medical Center

OTHER

lead

Virginia Commonwealth University

OTHER

NCT06747884 - Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension | Biotech Hunter | Biotech Hunter