36
Participants
Start Date
December 17, 2024
Primary Completion Date
December 31, 2026
Study Completion Date
December 31, 2026
ARO-ATXN2 Injection
single dose of ARO-ATXN2 by intrathecal (IT) administration
Placebo
calculated volume to match active treatment by IT administration
RECRUITING
Research Site, Sydney
RECRUITING
Research Site, Melbourne
RECRUITING
Research Site, Christchurch
RECRUITING
Research Site 2, Taipei
RECRUITING
Research Site 1, Kaohsiung City
RECRUITING
Research Site 2, Montreal
RECRUITING
Research Site 1, Montreal
RECRUITING
Research Site, Auckland
Lead Sponsor
Arrowhead Pharmaceuticals
INDUSTRY