Study of ARO-ATXN2 Injection in Adults With Spinocerebellar Ataxia Type 2

PHASE1RecruitingINTERVENTIONAL
Enrollment

36

Participants

Timeline

Start Date

December 17, 2024

Primary Completion Date

December 31, 2026

Study Completion Date

December 31, 2026

Conditions
Spinocerebellar Ataxia Type 2
Interventions
DRUG

ARO-ATXN2 Injection

single dose of ARO-ATXN2 by intrathecal (IT) administration

DRUG

Placebo

calculated volume to match active treatment by IT administration

Trial Locations (8)

2170

RECRUITING

Research Site, Sydney

3004

RECRUITING

Research Site, Melbourne

8011

RECRUITING

Research Site, Christchurch

112201

RECRUITING

Research Site 2, Taipei

833401

RECRUITING

Research Site 1, Kaohsiung City

H2X 0C1

RECRUITING

Research Site 2, Montreal

H3A 2B4

RECRUITING

Research Site 1, Montreal

0622

RECRUITING

Research Site, Auckland

Sponsors
All Listed Sponsors
lead

Arrowhead Pharmaceuticals

INDUSTRY