Repurposing Empagliflozin for DMD-associated Cardiomyopathy in Children 6-18 Years of Age

PHASE2Not yet recruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

October 1, 2025

Primary Completion Date

March 31, 2027

Study Completion Date

March 31, 2027

Conditions
DMD-associated Dilated Cardiomyopathy
Interventions
DRUG

Empagliflozin Tablets

Empagliflozin 10mg p.o. once daily (commercially available tablet)

Trial Locations (1)

WC1N 3JH

Great Ormond Street Hospital NHS Foundation Trust, London

All Listed Sponsors
collaborator

Great Ormond Street Hospital for Children NHS Foundation Trust

OTHER

collaborator

University College, London

OTHER

collaborator

Centre Hospitalier Universitaire Vaudois

OTHER

lead

Sebastiano Lava

OTHER