A Phase II Study of Intravitreal KIO-301 in Patients With Late-stage Retinitis Pigmentosa

PHASE2RecruitingINTERVENTIONAL
Enrollment

36

Participants

Timeline

Start Date

August 29, 2025

Primary Completion Date

August 31, 2027

Study Completion Date

August 31, 2027

Conditions
Retinitis Pigmentosa
Interventions
OTHER

Placebo (Sterile Saline or Balanced Salt Solution)

A control 50 μl injection of clear sterile saline or balanced salt solution (BSS) liquid.

DRUG

100 μg KIO-301

KIO-301 drug product is an ophthalmic formulation of the drug substance KIO-300-Cl in sulfobutylether-β-cyclodextrin, sucrose, phosphate buffer salts and water suitable for IVT injection. The drug substance KIO-300-Cl is a quaternary ammonium chloride salt of the active compound KIO-300.

DRUG

50 μg KIO-301

KIO-301 drug product is an ophthalmic formulation of the drug substance KIO-300-Cl in sulfobutylether-β-cyclodextrin, sucrose, phosphate buffer salts and water suitable for IVT injection. The drug substance KIO-300-Cl is a quaternary ammonium chloride salt of the active compound KIO-300.

Trial Locations (5)

2000

RECRUITING

Save Sight Institute, Sydney

3002

RECRUITING

Cerulea Clinical Trials, East Melbourne

4102

RECRUITING

Queensland Eye Institute, Woolloongabba

5000

NOT_YET_RECRUITING

Royal Adelaide Hospital, Adelaide

6009

RECRUITING

Lions Eye Institute, Nedlands

Sponsors
All Listed Sponsors
lead

Kiora Pharmaceuticals, Inc.

INDUSTRY

NCT06628947 - A Phase II Study of Intravitreal KIO-301 in Patients With Late-stage Retinitis Pigmentosa | Biotech Hunter | Biotech Hunter