300
Participants
Start Date
January 7, 2019
Primary Completion Date
December 31, 2033
Study Completion Date
December 31, 2033
Eteplirsen
No study medication will be provided by the Sponsor as a condition to participate in this observational study, and all decisions concerning each participant's treatment are at the discretion of the participant's treating physician. Participants will receive treatment as prescribed by the treating physician as part of standard of care.
Golodirsen
No study medication will be provided by the Sponsor as a condition to participate in this observational study, and all decisions concerning each participant's treatment are at the discretion of the participant's treating physician. Participants will receive treatment as prescribed by the treating physician as part of standard of care.
Casimersen
No study medication will be provided by the Sponsor as a condition to participate in this observational study, and all decisions concerning each participant's treatment are at the discretion of the participant's treating physician. Participants will receive treatment as prescribed by the treating physician as part of standard of care.
Columbia University Medical Center - PIN, New York
UPMC Children's Hospital of Pittsburgh, Pittsburgh
Children's Hospital of Philadelphia, Philadelphia
Children's National Hospital, Washington D.C.
Kennedy Krieger Institute, Baltimore
UVA Children's Hospital, Charlottesville
Atrium Health Wake Forest University Health Sciences, Winston-Salem
Duke Lenox Baker Children's Hospital, Durham
University of Florida, Gainesville
Nationwide Children's Hospital, Columbus
Children's Hospital Medical Center, Cincinnati
University Of Iowa Hospitals And Clinics, Iowa City
Washington University, St Louis
Arkansas Children's Hospital Research Institute, Little Rock
Cook Children's Hospital, Fort Worth
Texas Children's Hospital, Houston
Children's Hospital Los Angeles, Los Angeles
University of California Davis Medical Center, Sacramento
Seattle Children's Hospital, Seattle
Penn State Health Milton S. Hershey Medical Center, Hershey
Sarepta Therapeutics, Inc.
INDUSTRY