An Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its Long-Lasting Effects in DMD Patients (MUSCLE)

NARecruitingINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

November 6, 2024

Primary Completion Date

September 30, 2026

Study Completion Date

September 30, 2026

Conditions
Duchenne Muscular Dystrophin (DMD)
Interventions
GENETIC

HG302

Once intravenous injection; The duration of the study is about 32 weeks for each subject, including a 6 weeks screening period, enrollment visit, treatment visit, and 26 weeks follow-up period.

Trial Locations (1)

Unknown

RECRUITING

Shanghai Children s Medical Center Affiliated to Shanghai Jiao Tong University School of Medical, Shanghai

All Listed Sponsors
lead

HuidaGene Therapeutics Co., Ltd.

INDUSTRY