Registry and Natural History Study for Progressive Myoclonus Epilepsy Type 1 (EPM1)

RecruitingOBSERVATIONAL
Enrollment

200

Participants

Timeline

Start Date

October 10, 2024

Primary Completion Date

October 1, 2029

Study Completion Date

October 1, 2030

Conditions
Progressive Myoclonus Epilepsy Type 1EPM1CSTB-related DiseaseMyoclonus Epilepsies, ProgressiveUnverricht-Lundborg DiseaseProgressive Epilepsy and/or Ataxia With Myoclonus as a Major FeaturePMEProgressive Myoclonus-Epilepsies
Trial Locations (1)

02115

RECRUITING

Boston Childrens Hospital, Boston

All Listed Sponsors
collaborator

Epilepsy Foundation

OTHER

lead

Boston Children's Hospital

OTHER