A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMA

Enrolling by invitationOBSERVATIONAL
Enrollment

18

Participants

Timeline

Start Date

March 31, 2025

Primary Completion Date

September 10, 2030

Study Completion Date

December 31, 2030

Conditions
Spinal Muscular Atrophy
Interventions
OTHER

No intervention, only for observational studies

No intervention, only for observational studies

Trial Locations (1)

Unknown

The Children's Hospital of Fudan University, Shanghai

All Listed Sponsors
lead

Hangzhou Jiayin Biotech Ltd

INDUSTRY