Pegzilarginase in Subjects <24 Months Old With Arginase 1 Deficiency

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

3

Participants

Timeline

Start Date

August 30, 2024

Primary Completion Date

June 17, 2025

Study Completion Date

October 1, 2025

Conditions
Arginase 1 Deficiency
Interventions
DRUG

Pegzilarginase

SC administration of pegzilarginase over 12 weeks in subjects with ARG1-D who are \< 24 months of age

Trial Locations (3)

A-8036

Univ. Klinik für Kinder- und Jugendheilkunde Medizinische Universität, Graz

Unknown

Unidade de Doenças Metabólicas Pediatria, Hospital Santa Maria, Lisbon

BD9 6RJ

Bradford Royal Infirmary Duckworth Lane, Bradford

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Immedica Pharma AB

INDUSTRY

NCT06582524 - Pegzilarginase in Subjects <24 Months Old With Arginase 1 Deficiency | Biotech Hunter | Biotech Hunter