3
Participants
Start Date
August 30, 2024
Primary Completion Date
June 17, 2025
Study Completion Date
October 1, 2025
Pegzilarginase
SC administration of pegzilarginase over 12 weeks in subjects with ARG1-D who are \< 24 months of age
Univ. Klinik für Kinder- und Jugendheilkunde Medizinische Universität, Graz
Unidade de Doenças Metabólicas Pediatria, Hospital Santa Maria, Lisbon
Bradford Royal Infirmary Duckworth Lane, Bradford
Lead Sponsor
Immedica Pharma AB
INDUSTRY