NCT06564974 - Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy. | Biotech Hunter

Enrollment

250

Participants

Timeline

Start Date

July 31, 2024

Primary Completion Date

September 30, 2030

Study Completion Date

November 30, 2030

Conditions

Duchenne Muscular Dystrophy

Interventions

DRUG

Vamorolone

"Patients on treatment with Vamorolone (AGAMREE®) Dosage: Oral Suspension: 40 mg/mL . Per package insert, the recommended dosage is 6 mg/kg taken orally once daily, up to a maximum daily dosage of 300 mg for patients weighing more than 50 kg.~Decrease dosage gradually when administered for more than one week."

Trial Locations (25)

17033

RECRUITING

Penn State Milton S. Hershey Medical Center- Penn State Hershey Neuroscience Institute, Hershey

19104

RECRUITING

Children's Hospital of Philadelphia (CHOP), Philadelphia

22903

RECRUITING

University of Virginia Health System (UVAHS) - Pediatric Neuromuscular Center, Charlottesville

27710

RECRUITING

Duke University Medical Center and Childrens Health Center, Durham

28207

RECRUITING

Atrium Health Neurosciences Institute, Charlotte

32610

NOT_YET_RECRUITING

University of Florida Clinical and Translational Science Institue, Gainesville

32827

RECRUITING

Nemours Children's Hospital, Orlando

33155

RECRUITING

Nicklaus Children's Hospital, Miami

45229

RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

46202

NOT_YET_RECRUITING

Indiana University Health - Riley Hospital for Children, Indianapolis

49503

RECRUITING

Helen DeVos Children's Hospital, Grand Rapids

60611

RECRUITING

Lurie Children's Hospital of Chicago, Chicago

66205

RECRUITING

University of Kansas Medical Center, Kansas City

72202

RECRUITING

Arkansas Childrens Hospital, Little Rock

75235

RECRUITING

University of Texas Southwestern Medical Center, Dallas

76208

RECRUITING

Neurology Rare Disease Center - Neurology & Neuromuscular Care Center, Denton

78229

RECRUITING

The University of Texas Health Science Center at San Antonio, San Antonio

85016

RECRUITING

Phoenix Children's Hospital, Phoenix

90027

NOT_YET_RECRUITING

Children's Hospital Los Angeles, Los Angeles

94305

NOT_YET_RECRUITING

Stanford University, Palo Alto

95817

NOT_YET_RECRUITING

University of California, Davis, Sacramento

98105

RECRUITING

Seattle Children's Hospital, Seattle

01655

RECRUITING

University of Massachusetts Memorial Medical Center, North Worcester

00912

NOT_YET_RECRUITING

San Jorge Children's Hospital, San Juan

00927

RECRUITING

FDI Clinical Research, San Juan