NCT06532474View on ClinicalTrials.gov

Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

RecruitingOBSERVATIONAL
Enrollment

24

Participants

Timeline

Start Date

November 30, 2025

Primary Completion Date

September 30, 2026

Study Completion Date

March 31, 2027

Conditions
Spinal Muscular Atrophy
Trial Locations (1)

38105

RECRUITING

St. Jude Children's Research Hospital, Memphis

Sponsors

Collaborators (1)

Genentech, Inc.
All Listed Sponsors
collaborator

Genentech, Inc.

INDUSTRY

lead

St. Jude Children's Research Hospital

OTHER