A Long-term Follow-up Study in Participants Who Received CS-101

NARecruitingINTERVENTIONAL
Enrollment

5

Participants

Timeline

Start Date

June 18, 2024

Primary Completion Date

December 31, 2026

Study Completion Date

June 30, 2027

Conditions
Beta-Thalassemia
Interventions
GENETIC

CS-101

Autologous CD34+ hematopoietic stem cell suspension modified by in vitro base editing technique

Trial Locations (1)

201102

RECRUITING

Children's Hospital of Fudan University, Shanghai

All Listed Sponsors
lead

Children's Hospital of Fudan University

OTHER