A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)

PHASE2RecruitingINTERVENTIONAL
Enrollment

50

Participants

Timeline

Start Date

April 4, 2025

Primary Completion Date

November 30, 2026

Study Completion Date

November 15, 2027

Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG

Satralizumab

Satralizumab will be administered SC in the abdominal or femoral region on Day 1, Weeks 2 and 4 (loading doses) and then Q4W from Weeks 8 to 104 (maintenance doses) until the study completion visit.

Trial Locations (18)

10032

RECRUITING

Columbia University Medical Center, New York

16147

RECRUITING

IRCCS Istituto G. Gaslini, Genoa

20133

RECRUITING

Fondazione IRCCS Istituto Neurologico ?Carlo Besta?, Milan

23507

RECRUITING

Child's Hosp King's Daughters, Norfolk

30329

RECRUITING

Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta

33011

RECRUITING

Hospital U. Central de Asturias, Asturias

46026

RECRUITING

Hospital Universitario la Fe, Valencia

49503

RECRUITING

Corewell Health, Grand Rapids

72202

RECRUITING

Arkansas Children's Hospital, Little Rock

76208

RECRUITING

Neurology Rare Disease Center, Denton

01655

RECRUITING

University of Massachusetts Memorial Childrens Medical Center, Worcester

00168

RECRUITING

Policlinico Agostino Gemelli, Rome

93-338

RECRUITING

Instytut Centrum Zdrowia Matki Polki, ?ód?

80-952

RECRUITING

Uniwersyteckie Centrum Kliniczne, Gda?sk

60-355

RECRUITING

Uniwersytecki Szpital Kliniczny w Poznaniu, Późna

02-097

RECRUITING

Uniwersyteckie Centrum Kliniczne WUM, Centralny Szpital Kliniczny, Warsaw

08950

RECRUITING

Hospital Sant Joan De Deu, Esplugues de Llobregas

04009

RECRUITING

Hospital Universitario Torrecardenas;Servicio de Neurologia, Almería

All Listed Sponsors
lead

Hoffmann-La Roche

INDUSTRY