An Open Label Extension Study of CTI-1601 in Subjects With Friedreich's Ataxia

PHASE2Enrolling by invitationINTERVENTIONAL
Enrollment

75

Participants

Timeline

Start Date

January 25, 2024

Primary Completion Date

January 31, 2027

Study Completion Date

January 31, 2027

Conditions
Friedreich Ataxia
Interventions
BIOLOGICAL

CTI-1601

CTI-1601 is a recombinant fusion protein and is intended to deliver human frataxin, the protein deficient in Friedreich's ataxia

Trial Locations (7)

19104

Hospital of the University of Pennsylvania, Philadelphia

32608

Fixel Institute for Neurological Disease, University of Florida Health, Gainesville

33612

Morsani Center for Advanced Health Care, University of South Florida Health, Tampa

43210

Ohio State University United States, Columbus

52242

University of Iowa, Iowa City

90095

University of California Los Angeles, Los Angeles

07724

Clinilabs Drug Development, Corp., Eatontown

Sponsors
All Listed Sponsors
lead

Larimar Therapeutics, Inc.

INDUSTRY

NCT06447025 - An Open Label Extension Study of CTI-1601 in Subjects With Friedreich's Ataxia | Biotech Hunter | Biotech Hunter