14
Participants
Start Date
April 13, 2021
Primary Completion Date
April 11, 2023
Study Completion Date
February 28, 2027
rAAV2tYF-GRK1-RPGR
Adeno-associated virus vector expressing a human RPGR gene
University of Florida, Jacksonville
Cleveland Clinic, Cleveland
Cincinnati Eye Institute, Cincinnati
Retina Foundation of the Southwest, Dallas
Casey Eye Institute, Portland
Boston Children's Hosptial, Boston
Lead Sponsor
Beacon Therapeutics
INDUSTRY