Pharmacokinetic-guided Dosing of Emicizumab

PHASE4RecruitingINTERVENTIONAL
Enrollment

95

Participants

Timeline

Start Date

September 8, 2022

Primary Completion Date

March 31, 2026

Study Completion Date

August 31, 2026

Conditions
Hemophilia A With InhibitorHemophilia A Without InhibitorHemophilia A, SevereAdolescentChildAdult
Interventions
OTHER

Emicizumab - PK-guided dose reduction

PK-guided dose reduction emicizumab targeted at a Ctrough of 30μg/mL.

OTHER

Emicizumab - Dosis continuation group

Continue on their current dose regimen

OTHER

Emicizumab - Dose adjustment group

Adjusted in dosing regimen according to local protocol

Trial Locations (8)

6525 GA

RECRUITING

Radboud University Medical Center, Nijmegen

Unknown

RECRUITING

Maastricht University Medical Center, Maastricht

RECRUITING

University Medical Center Utrecht, Utrecht

1105 AZ

RECRUITING

Amsterdam University Medical Center, Amsterdam

2300 RC

RECRUITING

Leids Universitair Medisch Centrum, Leiden

3000CA

RECRUITING

Erasmus University Medical Center, Rotterdam

2545 CH

RECRUITING

HagaZiekenhuis, The Hague

9700 RB

RECRUITING

University Medical Center Groningen, Groningen

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Erasmus Medical Center

OTHER

collaborator

Amsterdam University Medical Center

OTHER

collaborator

Leiden University Medical Center

OTHER

collaborator

Radboud University Medical Center

OTHER

collaborator

Maastricht University Medical Center

OTHER

collaborator

University Medical Center Groningen

OTHER

collaborator

HagaZiekenhuis

OTHER

collaborator

Dutch Society of Haemophilia Patients

UNKNOWN

lead

Kathelijn Fischer

OTHER

NCT06320626 - Pharmacokinetic-guided Dosing of Emicizumab | Biotech Hunter | Biotech Hunter