8
Participants
Start Date
April 18, 2024
Primary Completion Date
May 31, 2025
Study Completion Date
July 31, 2025
CS-101 injection
Autologous CD34+ hematopoietic stem cell suspension modified by in vitro base editing technique
RECRUITING
The First Affiliated Hospital of Guangxi Medical University, Nanning
RECRUITING
Children's Hospital of Fudan University, Shanghai
RECRUITING
Ruijin Hospital Shanghai JiaoTong University School of Medicine, Shanghai
Lead Sponsor
CorrectSequence Therapeutics Co., Ltd
INDUSTRY