Trial Readiness and Endpoint Assessment in Congenital and Childhood Myotonic Dystrophy

CompletedOBSERVATIONAL
Enrollment

70

Participants

Timeline

Start Date

July 8, 2020

Primary Completion Date

April 1, 2024

Study Completion Date

April 1, 2024

Conditions
CDMChDM
Trial Locations (1)

20162

Fondazione Serena Onlus - Centro Clinico NeMO Milano, Milan

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Bambino Gesù Hospital and Research Institute

OTHER

collaborator

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

OTHER

collaborator

IRCCS Istituto delle Scienze Neurologiche di Bologna

OTHER

collaborator

IRCCS Fondazione Stella Maris

OTHER

collaborator

Fondazione Mondino

OTHER

collaborator

A.O.U. Città della Salute e della Scienza

OTHER

collaborator

Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta

OTHER

collaborator

Istituto Giannina Gaslini

OTHER

lead

Fondazione Serena Onlus - Centro Clinico NeMO Milano

OTHER

NCT06276244 - Trial Readiness and Endpoint Assessment in Congenital and Childhood Myotonic Dystrophy | Biotech Hunter | Biotech Hunter