A Study to Evaluate the Tolerability, Safety and Efficacy of VGM-R02b

PHASE1RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

April 29, 2024

Primary Completion Date

August 31, 2026

Study Completion Date

August 31, 2026

Conditions
Glutaric Acidemia Type IGlutaric Aciduria Type I
Interventions
BIOLOGICAL

VGM-R02b

Administered as specified in the treatment arm.

Trial Locations (1)

Unknown

RECRUITING

The Children's Hospital Zhejiang University Shcool of Medicine, Hangzhou

All Listed Sponsors
lead

Shanghai Vitalgen BioPharma Co., Ltd.

INDUSTRY