A Phase 1/2 Study to Investigate Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of HMB-001 in Glanzmann Thrombasthenia

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

57

Participants

Timeline

Start Date

December 13, 2022

Primary Completion Date

June 1, 2026

Study Completion Date

June 1, 2026

Conditions
Glanzmann Thrombasthenia
Interventions
DRUG

HMB-001

HMB-001 is a bispecific antibody being developed as a prophylactic treatment option to prevent and reduce bleeding events in patients with Glanzmann thrombasthenia.

Trial Locations (17)

15213

Hemophilia Center of Western Pennsylvania (HCWP) (Part B/C), Pittsburgh

55905

Mayo Clinic - Rochester (Part B/C), Rochester

70112

Tulane University Medical Center (Part B/C), New Orleans

92093

University of California, San Diego (UCSD) (Part B/C), La Jolla

98101

Washington Institute for Coagulation (Part B/C), Seattle

Unknown

University Hospital Leuven - Campus Gasthuisberg (Part B/C), Leuven

AP-HP Hopital Bicetre (Part B/C), Le Kremlin-Bicêtre

AP-HM - Hopital de la Timone, Marseille

AP-HP Hopital Necker-Enfants Malades (Part B/C), Paris

Azienda Ospedaliero-Universitaria Careggi (Part B/C), Florence

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano (Part B/C), Milan

Universitair Medisch Centrum Utrecht (Part B/C), Utrecht

Queen Elizabeth Hospital Birmingham (Part B/C), Birmingham

Leeds Teaching Hospitals NHS Trust, Leeds

Richmond Pharmacology Ltd (Part A/B/C), London

Royal Free London NHS Foundation Trust (Part B/C), London

The Royal London Hospital (Part B/C), Whitechapel

All Listed Sponsors
lead

Hemab ApS

INDUSTRY