Safety and Tolerability of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

9

Participants

Timeline

Start Date

July 2, 2022

Primary Completion Date

December 6, 2023

Study Completion Date

December 31, 2027

Conditions
Inherited Retinal Dystrophy Associated With RPE65 Mutations
Interventions
GENETIC

LX101

Subretinal Administration

Trial Locations (2)

Unknown

Beijing Tongren Hospital, Capital Medical University, Beijing

Shanghai General Hospital, Shanghai

All Listed Sponsors
lead

Innostellar Biotherapeutics Co.,Ltd

INDUSTRY