36
Participants
Start Date
February 20, 2024
Primary Completion Date
December 31, 2026
Study Completion Date
December 31, 2026
VX-670
Solution for intravenous administration.
Placebo
Solution for intravenous administration.
RECRUITING
University of Pennsylvania, Philadelphia
RECRUITING
Virginia Commonwealth University (Sanger Hall), Richmond
RECRUITING
Wake Forest Baptist Health, Winston-Salem
RECRUITING
University of Florida Clinical Research Center, Gainesville
RECRUITING
Washington University School of Medicine / St. Louis Children's Hospital, St Louis
RECRUITING
University of Kansas Medical Center, Fairway
RECRUITING
Stanford Neuromuscular Research, San Carlos
RECRUITING
Boston Children's Hospital, Boston
RECRUITING
Wesley Research Institute, Auchenflower
RECRUITING
Neuroscience Clinical Trials Unit, Alfred Brain, Melbourne
RECRUITING
Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg, Leuven
RECRUITING
Hopital de Chicoutimi, Chicoutimi
RECRUITING
Altasciences Montreal, Montreal
RECRUITING
McGIll University, Montreal
RECRUITING
University of Ottawa, Ottawa
RECRUITING
CHU Research Centre of Quebec, Québec
RECRUITING
Neuromuscular Reference Center Institute of Myology, Paris
RECRUITING
Ludwig Maximilians Universitaet Muenchen, München
RECRUITING
Centro Clinico NeMO, Milan
RECRUITING
Maastricht University Medical Center, Maastricht
RECRUITING
Hospital Universitario y Politécnico La Fe, Valencia
RECRUITING
Clinical Research Facility, Queen Elizabeth University Hospital, Glasgow
RECRUITING
Leonard Wolfson Experimental Neurology Centre CRF, London
RECRUITING
St. George's University Hospital, London
RECRUITING
Salford Royal Hospital, Salford
RECRUITING
Royal Hallamshire Hospital, Sheffield
Vertex Pharmaceuticals Incorporated
INDUSTRY