50
Participants
Start Date
July 26, 2023
Primary Completion Date
December 31, 2025
Study Completion Date
June 30, 2033
ANB-010, dose 1
Adeno-associated viral vector carrying the FVIII gene single infusion at dose 1.
ANB-010, dose 2
Adeno-associated viral vector carrying the FVIII gene single infusion at dose 2.
ANB-010, dose 3
Adeno-associated viral vector carrying the FVIII gene single infusion at dose 3.
"Federal State Budgetary Institution National Medical Research Centre for Hematology of the Ministry of Health of Russian Federation (Department of Clinical Diagnostics for Hematology and Hemostasis Disorders)", Moscow
"Federal State Budgetary Institution National Medical Research Centre for Hematology of the Ministry of Health of Russian Federation (Department of Traumatology and Reconstructive and Restorative Orthopedics for Patients with Hemophilia)", Moscow
Research Center for Hematology MHSD RF, Moscow
"Federal Budgetary Institution Moscow City Clinical Hospital named after S. P. Botkin", Moscow
"State Institution Komi Republican Oncological Dispensary", Syktyvkar
State budgetary healthcare institution Leningrad Regional Clinical Hospital, Gatchina
Russian Research Institute of Hematology and Transfusiology Federal State Institution of Federal Medical and Biological Agency, Saint Petersburg
City Polyclinic №37, Saint Petersburg
Almazov National Medical Research Centre, Saint Petersburg
"Federal State Budgetary Educational Institution of Higher Education Samara State Medical University of the Ministry of Healthcare of the Russian Federation", Samara
"Federal State Budgetary Educational Institution of Higher Education Bashkir State Medical University of the Ministry of Healthcare of the Russian Federation", Ufa
"State Autonomous Institution for Healthcare Chelyabinsk Regional Clinical Hospital", Chelyabinsk
"LLC Medis", Nizhny Novgorod
"Federal State Budgetary Organization of Science Kirov Research Institute of Hematology and Blood Transfusions of Federal Medical Biological agency", Kirov
"State Autonomous Institution for Healthcare of Sverdlovsk region Sverdlovsk Regional Clinical Hospital №1", Yekaterinburg
State Novosibirsk Regional Clinical Hospital, Novosibirsk
Kuzbass Clinical Hospital named after S.V. Belyaev, Kemerovo
Lead Sponsor
Biocad
INDUSTRY