40
Participants
Start Date
May 6, 2024
Primary Completion Date
May 6, 2027
Study Completion Date
May 6, 2031
SGT-003
Adeno-associated virus serotype SLB101 containing the human microdystrophin gene (h-µD5)
RECRUITING
Children's Hospital of the King's Daughters, Norfolk
RECRUITING
Rare Disease Research, Atlanta
RECRUITING
Nationwide Children's Hospital, Columbus
RECRUITING
Washington University in St. Louis, St Louis
RECRUITING
Arkansas Children's Hospital, Little Rock
RECRUITING
University of California, Los Angeles Medical Center, Los Angeles
RECRUITING
University of California, San Diego
RECRUITING
University of California, Davis, Sacramento
RECRUITING
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
RECRUITING
The Hospital for Sick Children, Toronto
RECRUITING
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
RECRUITING
Great Ormond Street Hospital, London
Solid Biosciences Inc.
INDUSTRY