NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia

EARLY_PHASE1RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

October 29, 2023

Primary Completion Date

November 30, 2024

Study Completion Date

November 30, 2028

Conditions
Homozygous Familial Hypercholesterolemia
Interventions
GENETIC

NGGT006

Single intravenous infusion of NGGT006 at dose 1 (7.5e12vg/kg), dose 2 (1.5e13vg/kg) , dose 3 (3e13vg/kg) and dose 4 (4e13vg/kg).

Trial Locations (1)

710061

RECRUITING

First Affiliated Hospital of Xian Jiaotong University, Xi'an

All Listed Sponsors
lead

First Affiliated Hospital Xi'an Jiaotong University

OTHER