Study to Assess the Safety, Tolerability, PK and PD of ABX1100

EARLY_PHASE1RecruitingINTERVENTIONAL
Enrollment

46

Participants

Timeline

Start Date

October 19, 2023

Primary Completion Date

December 31, 2025

Study Completion Date

December 31, 2025

Conditions
HealthyLate Onset Pompe Disease
Interventions
DRUG

ABX1100 injection for IV infusion

Centyrin protein-siRNA conjugate

DRUG

Placebo injection for IV infusion

placebo saline injection

Trial Locations (5)

22030

RECRUITING

Lysosomal and Rare Disorders Research and Treatment Center, Inc, Fairfax

63110

RECRUITING

Washington University School of Medicine, St Louis

92868

RECRUITING

UCI, Orange

Unknown

RECRUITING

MAGIC clinic, Calgary

RECRUITING

McMaster University, Hamilton

Sponsors
All Listed Sponsors
lead

Aro Biotherapeutics

INDUSTRY