A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4

RecruitingOBSERVATIONAL
Enrollment

100

Participants

Timeline

Start Date

February 13, 2024

Primary Completion Date

June 30, 2027

Study Completion Date

June 30, 2027

Conditions
Congenital Myasthenic Syndrome
Trial Locations (11)

1090

RECRUITING

Medical University of Vienna, Vienna

13385

RECRUITING

CHU Timone, Marseille

20133

RECRUITING

Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan

46026

RECRUITING

Hospital Universitari i Politecnic La Fe, Valencia

60611

RECRUITING

Ann and Robert H Lurie Children's Hospital of Chicago - Main Hospital, Chicago

62269

RECRUITING

Hospital Sisters Health System (HSHS) - St Elizabeth's Hospital, O'Fallon

75013

RECRUITING

Assistance Publique Hopitaux de Paris - Hopital Pitie-Salpetriere, Paris

95816

RECRUITING

UC Davis Health - UC Davis Health Midtown Ambulatory Care Center, Sacramento

K1Y 4E9

RECRUITING

The Ottawa Hospital - Civic Campus, Ottawa

BT16 1RH

RECRUITING

Ulster Hospital, Dundonald

OX3 9DU

RECRUITING

Oxford University Hospitals NHS Foundation Trust - John Radcliffe Hospital, Oxford

Sponsors

Lead Sponsor

All Listed Sponsors
lead

argenx

INDUSTRY