260
Participants
Start Date
November 2, 2023
Primary Completion Date
August 31, 2029
Study Completion Date
August 31, 2029
Sevasemten
Sevasemten is administered orally once per day
Rigshospitalet, Copenhagen
Universitaire Ziekenhuizen Leuven, Leuven
Centre Hospitalier Régional de la Citadelle, Liége
University Hospital Gent, Ghent
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille
University of Rochester Medical Center, Rochester
University of Pennsylvania, Philadelphia
Hospital Universitario Donostia, Donostia / San Sebastian
Fondazione IRCCS Ca'Granda Ospedale Maggiore, Milan
Kennedy Krieger Institute, Baltimore
Virginia Commonwealth University Health, Richmond
Rare Disease Research, LLC NC, Hillsborough
Rare Disease Research, Atlanta
University of Florida, Gainesville
Azienda Ospedale - Università Padova, Padua
Nationwide Children's Hospital, Columbus
CHU de Nantes, Nantes
University of Cincinnati Gardner Neuroscience Institute, Cincinnati
Hospital Universitari i Politecnic La Fe, Valencia
Indiana University School of Medicine, Indianapolis
University of Iowa, Iowa City
Northwestern University, Chicago
Washington University School of Medicine, St Louis
University of Kansas Medical Center, Kansas City
Arkansas Children's Hospital, Little Rock
AP-HP Hopital Pitie-Salpetriere, Paris
Neurology Rare Disease Center, Denton
National Neuromuscular Research Institute, Austin
UC Denver, Aurora
Klinikum der Ludwig-Maximilians-Universitaet Muenchen, Munich
UCLA Medical Center, Los Angeles
Hadassah University Hospital, Jerusalem
UC San Diego, La Jolla
UC Irvine Medical Center, Orange
Stanford Neuroscience Health Center, Palo Alto
UC Davis Medical Center, Sacramento
University of Massachusetts Memorial Medical Center, Worcester
CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice
Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore, Rome
Leids Universitair Medisch Centrum, Leiden
Hospital Universitario Vall d'Hebron, Barcelona
Hospital Universitario de Bellvitge, Barcelona
University College London Hospital, London
St. George's University Hospitals NHS Foundation Trust, London
Newcastle Freeman Hospital, Newcastle
Salford Royal Hospital, Salford
Lead Sponsor
Collaborators (1)
Medpace, Inc.
INDUSTRY
Edgewise Therapeutics, Inc.
INDUSTRY