28
Participants
Start Date
July 11, 2024
Primary Completion Date
January 31, 2026
Study Completion Date
January 31, 2026
LB54640
Oral daily administration
Placebo
Placebo matched to LB54640
Columbia University, New York
The University of North Carolina at Chapel Hill, Chapel Hill
St. Jude Children's Research Hospital, Memphis
University of Iowa Children's Hospital, Iowa City
Lynn Health Science Institute, Oklahoma City
Children's Hospital Colorado, Aurora
Tufts Medical Center, Boston
Birmingham Women's and Children's NHS Foundation Trust, Birmingham
University of Cambridge, Cambridge
Great Ormond Street Hospital for Children, London
Rhythm Pharmaceuticals, Inc.
INDUSTRY