32
Participants
Start Date
August 7, 2023
Primary Completion Date
April 2, 2030
Study Completion Date
April 2, 2030
SAR444836
Infusion pump, intravenous infusion (IV)
Investigational Site Number : 0320002, Ciudad Autonoma Buenos Aires
Medical University of SC- Site Number : 8400004, Charleston
University of Florida-Genetics- Site Number : 8400010, Gainesville
UHCMC- Site Number : 8400014, Cleveland
Investigational Site Number : 3760001, Tel Litwinsky
University of Texas- Site Number : 8400002, Houston
Children's Hospital IMD Clinic- Site Number : 8400015, Aurora
University of California San Francisco- Site Number : 8400007, San Francisco
Hospital de Clinicas de Porto Alegre - HCPA- Site Number : 0760001, Porto Alegre
UPMC Children's Hospital of Pittsburgh-4401 Penn Ave- Site Number : 8400018, Pittsburgh
Investigational Site Number : 7920001, Ankara
Lead Sponsor
Sanofi
INDUSTRY