A Phase 1/Phase 2 Open-label Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Intravenous Administration of SAR444836 in Adult Participants With Phenylketonuria

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

32

Participants

Timeline

Start Date

August 7, 2023

Primary Completion Date

April 2, 2030

Study Completion Date

April 2, 2030

Conditions
Phenylketonuria
Interventions
DRUG

SAR444836

Infusion pump, intravenous infusion (IV)

Trial Locations (11)

1199

Investigational Site Number : 0320002, Ciudad Autonoma Buenos Aires

29425

Medical University of SC- Site Number : 8400004, Charleston

32610

University of Florida-Genetics- Site Number : 8400010, Gainesville

44106

UHCMC- Site Number : 8400014, Cleveland

52621

Investigational Site Number : 3760001, Tel Litwinsky

77030

University of Texas- Site Number : 8400002, Houston

80045

Children's Hospital IMD Clinic- Site Number : 8400015, Aurora

94143

University of California San Francisco- Site Number : 8400007, San Francisco

90035903

Hospital de Clinicas de Porto Alegre - HCPA- Site Number : 0760001, Porto Alegre

15224-1334

UPMC Children's Hospital of Pittsburgh-4401 Penn Ave- Site Number : 8400018, Pittsburgh

06560

Investigational Site Number : 7920001, Ankara

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Sanofi

INDUSTRY