400
Participants
Start Date
September 27, 2023
Primary Completion Date
November 30, 2030
Study Completion Date
November 30, 2030
delandistrogene moxeparvovec
No study drug will be administered as part of this study. Eligible participants who received treatment with delandistrogene moxeparvovec during a previous clinical study will be included.
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
Universitair Ziekenhuis Gent, Neuromuscular Reference Centre (NMRC), Ghent
Columbia University Pediatric Neuromuscular Center, New York
University of Rochester Medical Center, Rochester
UOC Neurologia Pediatrica e Malattie Muscolari, Istituto G. Gaslini, Istituto Pediatrico di Ricovero e Cura a Carattere Scientifico, Genova
Chiildren's Hospital of Philadelphia, Philadelphia
UOC Neurologia, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
The Johns Hopkins Hospital, Rubenstein Child Health Bldg, Baltimore
Children's Hospital of The King's Daughters, Norfolk
Lenox Baker Children's Hospital (Duke University), Durham
University of Florida Clinical Research Center, Gainesville
Nationwide Children's Hospital, Columbus
Universitätsklinikum Essen - Klinik für Kinderheilkunde I, Essen
Hospital Universitario y Politecnico La fe. Neurology Department, Valencia
University of Iowa ICTS Clinical Research Unit, Iowa City
Children's Hospital Wisconsin, Milwaukee
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University School of Medicine, St Louis
Arkansas Children's Hospital, Little Rock
Children's Health Specialty Center, Dallas
University of Utah Health, Salt Lake City
UCLA Medical Center, Los Angeles
Rady Children's Hospital, San Diego
Lucile Packard Children's Hospital Stanford (LPCH), Palo Alto
University of California, Davis, Sacramento
Oregon Health and Science University, Portland
National Taiwan University Hospital, Taipei
Children's Hospital of Colorado, Aurora
Boston Children's Hospital, Boston
Hong Kong Children's Hospital, Hong Kong
UOC Neuropsichiatria Infantile, Area Salute del Bambino, Fondazione Policlinico Universitario A. Gemelli IRCCS, Universita Cattoclica del Sacro Cuore, Roma
Kobe University Hospital, Kobe
National Center of Neurology and Psychiatry, Kodaira
Hospital Sant Joan de Deu, Esplugues de Llobregat
Great Ormond Street Hospital For Children NHS Foundation Trust, London
Oxford University Hospitals NHS Foundation Trust, Oxford
Institute of Translational and Clinical Research, Newcastle upon Tyne
Hoffmann-La Roche
INDUSTRY
Sarepta Therapeutics, Inc.
INDUSTRY