NCT05933200View on ClinicalTrials.gov

A Study to Determine the Effect of Triheptanoin Compared With Even-Chain MCT on MCEs in Pediatric Patients With LC-FAOD

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

69

Participants

Timeline

Start Date

February 28, 2023

Primary Completion Date

August 31, 2027

Study Completion Date

August 31, 2027

Conditions
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
Interventions
DRUG

Triheptanoin

Liquid for oral (PO) or enteral feeding tube administration

DIETARY_SUPPLEMENT

MCT Oil

Liquid for oral (PO) or enteral feeding tube administration

Trial Locations (15)

11211

King Faisal Specialist Hospital & Research Centre, Riyadh

15706

University Hospital Santiago de Compostela, A Coruña

28041

University Hospital 12 de Octubre, Madrid

34093

Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi, Istanbul

34116

Cerrahpasa Medical Faculty, Istanbul

79106

Universitätsklinikum Freiburg, Freiburg im Breisgau

120-08

General University Hospital in Prague-GUH (Všeobecná fakultní nemocnice v Praze- VFN), Prague

113-8431

Juntendo University Hospital, Bunkyo City

Unknown

The Jikei University Hospital, Minato

Cukurova University, Adana

Gazi University, Ankara

Ege University, Bornova-İzmir

04-730

Instytut Pomnik-Centrum Zdrowia Dziecka, Warsaw

80-952

Gdańksi Uniwersytet Medyczny, Gdansk

08950

Sant Joan de Deu Hospital (SJD), Barcelona

All Listed Sponsors
lead

Ultragenyx Pharmaceutical Inc

INDUSTRY