Combination Regimen With Sodium Valproate for Severe Hemophilia: a Single-arm, Phase 1, Pilot Trial.

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

April 1, 2022

Primary Completion Date

April 1, 2025

Study Completion Date

April 1, 2025

Conditions
Hemophilia
Interventions
DRUG

Sodium valproate extended-release tablets

Sodium valproate extended-release tablets 0.5g/day; sirolimus tablets 1mg/day and calcitriol capsules 0.25μg/day.

Trial Locations (1)

100853

RECRUITING

PLA General Hospital, Beijing

All Listed Sponsors
lead

Xue-chun Lu

OTHER