Gene Therapy for Subjects With RPGR Mutation-associated X-linked Retinitis Pigmentosa

EARLY_PHASE1RecruitingINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

February 1, 2023

Primary Completion Date

October 31, 2023

Study Completion Date

November 1, 2027

Conditions
X-Linked Retinitis Pigmentosa
Interventions
GENETIC

FT-002

Comparison of different dosages of FT-002

Trial Locations (2)

100142

RECRUITING

Peking Union Medical College Hospital, Beijing

200032

RECRUITING

Eye & ENT hospital of Fudan university, Shanghai

Sponsors
All Listed Sponsors
collaborator

Eye & ENT Hospital of Fudan University

OTHER

collaborator

Peking Union Medical College Hospital

OTHER

collaborator

Henan Provincial People's Hospital

OTHER

lead

Frontera Therapeutics

INDUSTRY