28
Participants
Start Date
August 14, 2024
Primary Completion Date
March 31, 2028
Study Completion Date
March 31, 2029
Risdiplam
Participants will receive risdiplam orally at the currently approved dose. The dose should be adapted for weight and age.
RECRUITING
Charité - Universitätsmedizin Berlin SPZ Abteilung Neuropaediatrie, Berlin
RECRUITING
Children'S Hospital of Philadelphia, Philadelphia
RECRUITING
Children's Hospital of the King's Daughter, Norfolk
RECRUITING
University of Florida Pediatrics, Gainesville
RECRUITING
UKGM Standort Gießen, Giessen
RECRUITING
Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids
RECRUITING
University of Arkansas for Medical Sciences, Little Rock
RECRUITING
University of Texas Southwestern Medical Center, Dallas
RECRUITING
Children's Hospital of Colorado, Aurora
RECRUITING
Valley Children's Hospital, Madera
RECRUITING
Stanford Univ Medical Center, Palo Alto
RECRUITING
Schneider Children's Medical Center of Israel, Petah Tikva
RECRUITING
Sourasky MC, Dana-Dwek Children's Hospital, Tel Aviv
RECRUITING
Soroka Medical Center, Beersheba
RECRUITING
Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
RECRUITING
Uniwersyteckie Centrum Kliniczne, Gdansk
RECRUITING
Instytut Pomnik Centrum Zdrowia Dziecka, Warsaw
RECRUITING
Sidra Medicine, Al Rayyan
RECRUITING
Great Ormond Street Hospital For Children, London
Hoffmann-La Roche
INDUSTRY