28
Participants
Start Date
May 30, 2024
Primary Completion Date
March 31, 2028
Study Completion Date
March 31, 2029
Risdiplam
Participants will receive risdiplam orally at the currently approved dose. The dose should be adapted for weight and age.
RECRUITING
Columbia University Medical Center, New York
RECRUITING
Charité - Universitätsmedizin Berlin SPZ Abteilung Neuropaediatrie, Berlin
RECRUITING
Children'S Hospital of Philadelphia, Philadelphia
RECRUITING
Children's Hospital of the King's Daughter, Norfolk
RECRUITING
University of Florida Pediatrics, Gainesville
RECRUITING
UKGM Standort Gießen, Giessen
RECRUITING
Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids
NOT_YET_RECRUITING
Ann and Robert H. Lurie Children Hospital of Chicago, Chicago
RECRUITING
University of Arkansas for Medical Sciences, Little Rock
RECRUITING
The University of Texas Southwestern Medical Center at Dallas, Dallas
RECRUITING
Cook Children's Jane and John Justin Neurosciences Center, Fort Worth
RECRUITING
Children's Hospital of Colorado, Aurora
RECRUITING
Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
RECRUITING
Uniwersyteckie Centrum Kliniczne, Gda?sk
RECRUITING
Instytut Pomnik Centrum Zdrowia Dziecka, Warsaw
RECRUITING
Great Ormond Street Hospital For Children, London
Hoffmann-La Roche
INDUSTRY