Pharmacokinetics, Pharmacodynamics and Safety of Epeleuton in Patients With Sickle Cell Disease

PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

30

Participants

Timeline

Start Date

January 10, 2024

Primary Completion Date

February 28, 2026

Study Completion Date

March 31, 2026

Conditions
Sickle Cell Disease
Interventions
DRUG

Epeleuton

Participants will receive 2000mg Epeleuton (DS102) capsules twice daily.

Trial Locations (21)

10461

Jacobi Medical Center, The Bronx

11432

Queens Hospital Center, Jamaica

20010

Medstar Health, Washington D.C.

20774

Kaiser Permanente Mid-Atlantic States, Largo

20817

The Center for Cancer and Blood Disorders, A Division of American Oncology Partners, PA, Bethesda

21205

The Johns Hopkins University School of Medicine, Baltimore

27517

UNC Health, Chapel Hill

27560

Science 37, Morrisville

27834

East Carolina University, Greenville

30303

Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta at Hughes Spalding, Atlanta

Emory University - Georgia Comprehensive Sickle Cell Center, Atlanta

30329

Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta at Arthur M. Blank Hospital, Atlanta

35294

University of Alabama at Birmingham (UAB), Birmingham

48201

Karmanos Cancer Institute, Detroit

60612

UI Health Sickle Cell Center, Chicago

06030-1163

New England Sickle Cell Institute, UConn Health, Farmington

08901

Robert Wood Johnson Medical School Rutgers, New Brunswick

07112

Newark Beth Israel Medical Center, Newark

T2N 2T9

Foothills Medical Center, Calgary

V6E 1M7

St Paul's Hospital Hematology/Oncology Research, Vancouver

M5G 2C4

Toronto General Hospital, Toronto

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Afimmune

INDUSTRY

NCT05861453 - Pharmacokinetics, Pharmacodynamics and Safety of Epeleuton in Patients With Sickle Cell Disease | Biotech Hunter | Biotech Hunter