Safety Evaluation of Gene Therapy Drug in the Treatment of Primary Hypertriglyceridemic Patients With Recurrent Pancreatitis

PHASE1RecruitingINTERVENTIONAL
Enrollment

7

Participants

Timeline

Start Date

September 20, 2024

Primary Completion Date

December 31, 2026

Study Completion Date

December 31, 2028

Conditions
Hypertriglyceridemia, Familial
Interventions
GENETIC

GC304

Self-complementary adeno-associated virus serotype 5 (AAV5) carrying a codon-optimized LPL coding sequence(coLPL) driven by a liver-specific promoter (LP)

Trial Locations (1)

Unknown

RECRUITING

Peking Union Medical College, Beijing

All Listed Sponsors
lead

GeneCradle Inc

INDUSTRY