20
Participants
Start Date
April 12, 2024
Primary Completion Date
September 30, 2026
Study Completion Date
September 30, 2026
Vosoritide
Vosoritide administered daily via subcutaneous injection for 12 months using the FDA approved weight-based dosing band strategy for achondroplasia.
RECRUITING
Children's National Hospital, Washington D.C.
Roopa Kanakatti Shankar, MBBS, MS
OTHER