Evaluation of Long-Term Safety and Efficacy of Vanzacaftor/Tezacaftor/Deutivacaftor in Cystic Fibrosis Participants 1 Year of Age and Older

PHASE3Enrolling by invitationINTERVENTIONAL
Enrollment

174

Participants

Timeline

Start Date

August 11, 2023

Primary Completion Date

July 30, 2029

Study Completion Date

July 30, 2029

Conditions
Cystic Fibrosis
Interventions
DRUG

VNZ/TEZ/D-IVA

Fixed-dose combination tablets or granules for oral administration.

Trial Locations (32)

11042

Cohen Children's Medical Center - Lakeville Road, Lake Success

15224

Children's Hospital of Pittsburgh - Pulmonology, Pittsburgh

30322

The Emory Clinic - Clifton Road - Pulmonology, Atlanta

43205

Nationwide Children's Hospital, Columbus

44106

UH Cleveland Medical Center - Pulmonology, Cleveland

45229

Cincinnati Children's Hospital Medical Center - Pulmonology, Cincinnati

46202

JW Riley Hospital for Children - Pulmonology, Indianapolis

55404

Children's Respiratory and Critical Care Specialists, P.A., Children's Hospitals and Clinics of Minnesota, Minneapolis

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

63110

St. Louis Children's Hospital - Pulmonology, St Louis

64108

The Children's Mercy Hospital, Kansas City

77030

Texas Children's Hospital - Wallace Tower - Pulmonology, Houston

80045

Children's Hospital of Colorado - Pulmonology, Aurora

92868

Children's Hospital of Orange County, Orange

94304

Stanford University - Palo Alto - Pulmonology, Palo Alto

02115

Boston Children's Hospital, Boston

05446

Vermont Lung Center, Colchester

02212

American Family Childrens Hospital, Madison

Unknown

Women & Children's Hospital, North Adelaide

Murdoch Children's Research Institute (MCRI) - Pulmonology, Parkville

Children's Health Queensland Hospital and Health Service, South Brisbane

Hopital Femme Mere-Enfant, Bron

Hopital Necker Enfants Malades - Pulmonology, Paris

Charite Paediatric Pulmonology Department, Berlin

Universitatsklinikum Essen, Essen

Medizinische Hochschule Hannover, Hanover

Sophia Children's Hospital, Rotterdam

Sahlgrenska Universitetssjukhuset - Göteborg CF-center, Gothenburg

Inselspital Bern, Bern

Kinderspital Zurich - Abteilung Pneumologie, Zurich

Noah's Ark Children's Hospital for Wales, Cardiff

Great Ormond Street Hospital for Children, London

All Listed Sponsors
lead

Vertex Pharmaceuticals Incorporated

INDUSTRY