10
Participants
Start Date
April 26, 2024
Primary Completion Date
April 17, 2026
Study Completion Date
April 17, 2026
Risdiplam
Participants will receive 0.15 mg/kg risdiplam orally once daily for 28 days.
RECRUITING
Hopital Universitaire des Enfants Reine Fabiola, Brussels
RECRUITING
UMC Utrecht, Utrecht
RECRUITING
CHR Citadelle, Liège
RECRUITING
Clinic for Special Children., Gordonville
RECRUITING
Fondazione Serena Onlus - CENTRO CLINICO NEMO, Milano
RECRUITING
Universitatsklinikum Essen, Essen
RECRUITING
University Of Michigan, Ann Arbor
RECRUITING
Ann and Robert H. Lurie Children Hospital of Chicago, Chicago
RECRUITING
Children'S Hospital of Eastern Ontario, Ottawa
RECRUITING
Fondazione Policlinico Univeristario A. Gemelli, ROMA
RECRUITING
OUS (Oslo University Hospital), Rikshospitalet, Oslo
RECRUITING
Uniwersyteckie Centrum Kliniczne, Gda?sk
RECRUITING
Instytut Pomnik - Centrum Zdrowia Dziecka, Warsaw
Hoffmann-La Roche
INDUSTRY