A Retrospective Study to Characterize Participants With Propionic Acidemia

Active, not recruitingOBSERVATIONAL
Enrollment

60

Participants

Timeline

Start Date

June 16, 2023

Primary Completion Date

August 31, 2026

Study Completion Date

August 31, 2026

Conditions
Propionic Acidemia
Trial Locations (25)

3052

Royal Children's Hospital Melbourne, Parkville

8950

Hospital Sant Joan de Deu, Esplugues de Llobregat

13386

CHU de Marseille - Hôpital de la Timone, Marseille

19104

Children's Hospital of Philadelphia, Philadelphia

20900

ASST di Monza - Azienda Ospedaliera San Gerardo, Monza

28034

Hospital Universitario Raymon y Cajal, Madrid

28041

Hospital Universitario 12 de Octubre, Madrid

31300

CHU Toulouse, Toulouse

39008

Hospital Universitario Marques de Valdecilla, Santander

41013

Hospital Universitario Virgen del Rocio - PPDS, Seville

46026

Hospital Universitari I Politecnic La Fe de Valencia, Valencia

48903

Hospital Universitario Cruces, Barakaldo

50139

Azienda Ospedaliero Universitaria A Meyer - INCIPIT - PIN, Florence

75743

Hôpital Necker - Enfants Malades, Paris

80131

Azienda Ospedaliera Universitaria Federico II, Napoli

94305-2200

University of Stanford Medical Center, Stanford

21287-0010

Johns Hopkins University, Baltimore

48109-5000

University of Michigan Hospital, Ann Arbor

77030-2614

Texas Children's Hospital, Houston

98105-3901

Seattle Children's Hospital, Seattle

T6G 2B7

Stollery Children's Hospital University of Alberta, Edmonton

3015 GD

Erasmus MC, Rotterdam

Unknown

St Mary's Hospital - PPDS, Manchester

Great Ormond Street Hospital, City of London

B29 6JD

University Hospital Birmingham, Birmingham

All Listed Sponsors
lead

ModernaTX, Inc.

INDUSTRY