Setrusumab vs Bisphosphonates in Pediatric Subjects With Osteogenesis Imperfecta

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

69

Participants

Timeline

Start Date

June 14, 2023

Primary Completion Date

March 31, 2026

Study Completion Date

April 30, 2027

Conditions
Osteogenesis Imperfecta
Interventions
DRUG

Bisphosphonate

Administered per investigator discretion via intravenous (IV) infusion

BIOLOGICAL

Setrusumab

A fully human sclerostin neutralizing monoclonal antibody (mAb) administered once a month (QM) via intravenous (IV) infusion

Trial Locations (20)

19803

Nemours/ Alfred i. duPoint Hospital for Children, Wilmington

20010

Children's National Hospital DC, Washington D.C.

27599

University of North Carolina at Chapel Hill (UNC), Chapel Hill

33612

University of South Florida, Tampa

37212

Vanderbilt University Medical Center (VUMC), Nashville

60707

Shriners Hospitals for Children Chicago, Chicago

63110

Washington University School of Medicine, St Louis

75015

Institut Imagine, Paris

76104

Cook Children's Medical Center, Fort Worth

77030

Baylor College of Medicine, Houston

80045

Children's Hospital Colorado, Aurora

85206

Phoenix Children's Hospital, Phoenix

90027

Childrens Hospital LA, Los Angeles

06510

Yale New Haven Hospital, New Haven

90035-903

Hospital de Clinicas de Porto Alegre (HCPA), Porto Alegre

N6A 5W9

Children's Hospital at London Health Sciences Centre, London

KIH 8L1

Childrens Hospital Of Eastern Ontario Research Institute, University Of Ottawa, Ottawa

00161

Azienda Ospedaliera Universitaria Policlinico Umberto I, Roma

3584 EA

Universitair Medisch Centrum Utrecht (UMCU) - Wilhelmina Kinderziekenhuis, Utrecht

91-738

Uniwersytet Medyczny w Lodzi - Klinika Endokrynologii i Chorob Metabolicznych, Lodz

All Listed Sponsors
lead

Ultragenyx Pharmaceutical Inc

INDUSTRY